“Why not me?”: Many SMA patients left without access to disease-modifying medicines due to age, geography

Teaching by example: How Alex learned self-advocacy through rare kidney disease

Membranoproliferative glomerulonephritis

Alex was on maternity leave from her career in the classroom when she was diagnosed with MPGN, an ultra-rare kidney disease that threatened her future as both a teacher and a mom.

Understanding C3G and IC-MPGN

Patient Voice spoke with Dr. Jocelyn Garland to learn about two ultra-rare forms of kidney disease that can lead to kidney failure if untreated: C3 glomerulopathy (C3G) and immune complex-mediated membranoproliferative glomerulonephritis (IC-MPGN).

Connecting the dots: How AI is unlocking new potential in rare disease diagnosis, treatment, and support

AI tools are helping patients, caregivers, and clinicians make sense of complex health data — and turn insights into action.